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Welcome to the CRISPR revolution. Take a break and join us as we guide conversations with an expert CRISPR cast about this cutting-edge science.
Stephanie Cherqui Discusses Clinical Development of CRISPR Therapies for Rare Diseases
CRISPR Cuts
20 minutes 27 seconds
2 years ago
Stephanie Cherqui Discusses Clinical Development of CRISPR Therapies for Rare Diseases
Professor Stephanie Cherqui, UCSD, has worked on the development of cell therapies for two rare genetic diseases, cystinosis and Friedreich’s ataxia. In this interview, Dr. Cherqui chats about her experience working on rare diseases, developing a CRISPR-edited therapy for Friedreich's ataxia, navigating regulatory challenges in cell and gene therapies, and more.
CRISPR Cuts
Welcome to the CRISPR revolution. Take a break and join us as we guide conversations with an expert CRISPR cast about this cutting-edge science.