Professor Amit Nathwani’s journey to create a one-shot cure for haemophilia A

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UCLB Big Talks on Big Impacts

UCL Minds

13 episodes

1 week ago

From chronic diseases, the climate crisis, to social injustice, how are we tackling the biggest problems of the 21st century? As UCL Business (UCLB) celebrates its 30th anniversary in 2023, this new monthly podcast series will explore how we have supported UCL academics to create impact across several areas, such as: medical research, patient healthcare, the environment, and our wellbeing in a contemporary society. New episodes will be released every third Thursday of each month. Soundtrack by Harry Penfold and Thomas Shearwood.

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Education

Health & Fitness

Professor Amit Nathwani’s journey to create a one-shot cure for haemophilia A

UCLB Big Talks on Big Impacts

23 minutes

1 year ago

Professor Amit Nathwani’s journey to create a one-shot cure for haemophilia A

To mark World Haemophilia Day, we sit down with Professor Amit Nathwani of the UCL Cancer Institute to explore his journey to commercialising the groundbreaking haemophilia A treatment, Roctavian. Host Nigel Campbell is joined by Prof Nathwani and Dr. Rick Fagan, UCLB Director of Biopharm, to explore how Amit’s work looking after patients with haemophilia in the NHS instilled a mission to develop a 'one and done' vaccine type approach to the condition. Amit’s lab to market story, working with UCLB, led to the creation of Roctavian, a one-time gene therapy used for the treatment of adults with severe haemophilia A. The therapy, which was licensed to BioMarin Pharmaceutical Inc, received marketing approval in Europe in 2022 and US FDA approval in 2023, and is now available to patients commercially.

Date of episode recording: 2024-04-10T00:00:00Z
Duration: 00:23:58
Language of episode: English
Presenter: Nigel Campbell
Guests: Prof Amit Nathwani; Dr Rick Fagan
Producer: Nora Amin

Visit out website for the transcript: https://www.uclb.com/